Our mRNAi GOLD™ is a platform for precision engineered therapies designed to accurately target and ‘silence’ specific disease-associated genes in liver cells by using the body’s natural process of RNA interference (RNAi).
- Improves molecular design
- Maximizes efficacy
- Minimizes off-target effects
- Stabilizes molecules
- Optimizes manufacturing
- Robust and growing IP estate
High-quality discovery programs